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| Drug & Indication | Stage & Event | Catalyst Date |
|---|---|---|
Empaveli (systemic pegcetacoplan) (APL-2) Details Paroxysmal nocturnal hemoglobinuria | Approved Quarterly sales | |
EMPAVELI® (pegcetacoplan) Details Immune complex membranoproliferative glomerulonephritis, C3 Glomerulopathy | Approved Quarterly sales | |
SYFOVRE™ (Intravitreal pegcetacoplan) Details Geographic atrophy, Age-related macular degeneration | Approved Quarterly sales | |
EMPAVELI/pegcetacoplan (APL-2) (C3 Inhibitor) Details Delayed Graft Function | Phase 3 Initiation | |
EMPAVELI/pegcetacoplan (APL-2) (C3 Inhibitor) Details Focal Segmental Glomerulosclerosis | Phase 3 Initiation | |
Systemic pegcetacoplan (APL-2) Details Hematopoietic stem cell transplantation thrombotic microangiopathies | Phase 2 Data readout | |
APL-3007 + SYFOVRE Details Geographic atrophy (GA) | Phase 2 Data readout | |
Systemic pegcetacoplan (APL-2) Details Immune complex membranoproliferative glomerulonephritis, C3 Glomerulopathy | Phase 2 Update | |
Intravenous APL-9 Details ARDS (Acute respiratory distress syndrome), TMA (Thrombotic microangiopathies) | Failed Discontinued | |
Systemic pegcetacoplan (APL-2) Details Cold agglutinin disease | Failed Discontinued | |
Systemic pegcetacoplan (APL-2) Details Amyotrophic lateral sclerosis | Failed Discontinued |
